The FDA has cleared PTC Ther­a­peu­tics’ gene ther­a­py for AADC de­fi­cien­cy, an ul­tra-rare dis­ease that im­pacts the ...
A Brisbane father has died after being diagnosed with an extremely rare and incurable disease that he dubbed the family ...
to use its artificial intelligence to identify novel rare disease indications for a discontinued drug asset. Under the terms of the agreement, Sanofi will provide data related to the unnamed drug ...
The brother of former Channel Nine reporter Hayley Webb has died from a rare brain disease. Lachlan Webb, who is the younger ...
High blood pressure is a rare health issue among teens, but U.S. case numbers are creeping upwards. Now, research published ...
As a wave of patent expirations encroaches upon many of the world’s top drugmakers, companies will need to be diligent in ...
A slow launch for Alzheimer's medicine Leqembi, a lackluster pipeline and a challenging drug launch environment are just a ...
California’s recent decision to create a Rare Disease Advisory Council is a milestone that brings new hope to people living ...
The combined net Q3 2024 revenue of approximately $3.1 million for prescription and non-prescription products, including license revenue, increased approximately 14% versus net Q2 2024 revenue of $2.7 ...
New puppies are usually put on preventative for heartworm disease when they go in for their vaccines. If your dog was not ...
Video: Tulsa man with rare muscle disease is gifted a new car and RV to travel the country ...
In Tulsa, mechanic Matt Parker rallied the community to support 21-year-old Corbin Norcom, who has a fatal disease, by ...